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A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
Representative Western gel blot showing CRIM negative s | Open-i
Frontiers | Recommendations for Infantile-Onset and Late-Onset Pompe Disease: An Iranian Consensus
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction - ScienceDirect
Immunological challenges and approaches to immunomodulation in Pompe disease: a literature review. - Abstract - Europe PMC
Pompe disease treatment: What are the options? | Pompe Disease News
Child Neurology: Pompe disease | Neurology
Algorithm for the Early Diagnosis and Treatment of Patients with Cross Reactive Immunologic Material-Negative Classic Infantile Pompe Disease: A Step towards Improving the Efficacy of ERT | PLOS ONE
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine
The impact of antibodies on clinical outcomes in diseases treated with therapeutic protein: Lessons learned from infantile Pompe disease | Genetics in Medicine
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy | Genetics in Medicine
Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy - ScienceDirect
Frontiers | A Race Against Time—Changing the Natural History of CRIM Negative Infantile Pompe Disease
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
Algorithm for the Early Diagnosis and Treatment of Patients with Cross Reactive Immunologic Material- Negative Classic Infantile
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
Early ERT Key in Severe Classic Infantile Pompe, Study Finds
Enzyme therapy and immune response in relation to CRIM status: the Dutch experience in classic infantile Pompe disease | Journal of Inherited Metabolic Disease
Efficacy of ERT+ITI in CRIM-negative IPD patients treated in the... | Download Table
PDF) Successful Immune Tolerance Induction to Enzyme Replacement Therapy in CRIM-Negative Infantile Pompe Disease